hATTR-PN

Symptoms related to familial amyloid polyneuropathy (FAP) and other forms of hereditary transthyretin (ATTR) amyloidosis were found in…

Caring for a loved one with a rare disease, especially during these uncertain times, demands significant time, attention, patience, and dedication. To help meet that…

Familial amyloid polyneuropathy (FAP) leads to the formation and accumulation of abnormal protein clumps or amyloids. This accumulation can cause issues in a number of…

AT-01, an imaging agent being developed by Attralus, can help to differentiate between transthyretin (ATTR) amyloidosis — which includes familial amyloid polyneuropathy (FAP)…

It is a summer morning here in New Zealand. As I write this, a cool, gentle breeze blows through the house, and I am being…

Familial amyloid polyneuropathy (FAP) is a progressive disorder that can lead to multiple health issues that affect your everyday life. Here are some ways…

Vutrisiran, a second-generation RNA interference (RNAi) therapy candidate, safely and effectively reduces neurologic impairment and improves physical function and quality of life in adults…

Sleep is an essential part of life that comes so naturally, from the moment we come into being. Yet sometimes we forget the impact that…

The National Organization for Rare Disorders (NORD) is seeking individuals willing to share real-life experiences with rare diseases to speak at its upcoming virtual…

Benzbromarone (BBM), a medicine used to treat gout, can stabilize the TTR protein to the same degree as therapies used…