hATTR-PN

In his book “1984,” George Orwell wrote, “Of pain you could wish only one thing: that it should stop. Nothing in…

Nerve function deteriorates more rapidly in people with familial amyloid polyneuropathy (FAP) than in those with other peripheral…

As I write this, my husband, Aubrey, is undergoing surgery to remedy his congested nasal passages, which have reduced the oxygen flow into his lungs.

Scientist Jonathan Wall, PhD, has won a $1.79-million grant to develop a potential treatment for amyloidosis, a group of conditions that includes familial amyloid…

Ionis Pharmaceuticals has launched a new grant program to fund novice researchers investigating transthyretin (ATTR) amyloidosis, a group of conditions that includes familial…

Leading an association that supports and advocates for rare disease patients while being a caregiver to one certainly has shaped my outlook on life. To…

The symptoms of familial amyloid polyneuropathy (FAP) may make it harder to enjoy a good night’s sleep. To help you sleep better, in addition to…

Many diseases have their own awareness color — breast cancer is pink, muscular dystrophy is green, and AIDS is red, for example — but…

Intellia Therapeutics anticipates reporting interim data this year from a Phase 1 study evaluating the safety and activity profile of…

Familial amyloid polyneuropathy (FAP) is a rare genetic disorder caused by the buildup of abnormal protein clumps called amyloids throughout the body. These amyloids…